Metadata
- Name
- Outcome Measures in Duchenne Muscular Dystrophy: A Natural History Study
- Repository
- ClinicalTrials.gov
- Identifier
- clinicaltrials:NCT02780492
- Description
- Novel emerging therapies for Duchenne Muscular Dystrophy (DMD) require a deeper understanding
of DMD natural history. This study aim to assess the natural history of DMD through a
composite assessment tool capable of capturing disease progression linking ambulant and
non-ambulant phases of the disease. - Data or Study Types
- clinical trial
- Keywords
- Myoset, Natural history, North Star Ambulatory Assessment (NSAA), 6 minute walk distance (6MWD), Exon skipping, Duchenne muscular dystrophy, Outcome measures
- Source Organization
- Unknown
- Access Conditions
- available
- Year
- 2016
- Access Hyperlink
- https://clinicaltrials.gov/ct2/show/NCT02780492
Distributions
- Encoding Format: HTML ; URL: https://clinicaltrials.gov/ct2/show/results/NCT02780492