Metadata
- Name
- Experimental Gene Transfer Procedure to Treat Alpha 1-Antitrypsin Deficiency
- Repository
- ClinicalTrials.gov
- Identifier
- clinicaltrials:NCT00377416
- Description
- Individuals with a deficiency of the Alpha 1-antitrypsin (AAT) protein are at risk for
developing emphysema and liver damage. Researchers have developed a way to introduce normal
AAT genes into muscle cells so that the AAT protein is produced at normal levels. This study
will evaluate the safety of the experimental gene transfer procedure in individuals with AAT
deficiency. - Data or Study Types
- clinical trial
- Keywords
- Gene Transfer Techniques, Gene Therapy
- Source Organization
- Unknown
- Access Conditions
- available
- Year
- 2006
- Access Hyperlink
- https://clinicaltrials.gov/ct2/show/NCT00377416
Distributions
- Encoding Format: HTML ; URL: https://clinicaltrials.gov/ct2/show/results/NCT00377416