Metadata
- Name
- Phase I/II Study of SRP-4053 in DMD Patients
- Repository
- ClinicalTrials.gov
- Identifier
- clinicaltrials:NCT02310906
- Description
- This is a first-in-human, multiple-dose 2-part study to assess the safety, tolerability,
efficacy, and pharmacokinetics of SRP-4053 in Duchenne muscular dystrophy (DMD) patients with
deletions amenable to exon 53 skipping. - Data or Study Types
- clinical trial
- Keywords
- Exon 53, DMD, Exon Skipping, Pediatric, Duchenne muscular dystrophy, Ambulatory
- Source Organization
- Unknown
- Access Conditions
- available
- Year
- 2014
- Access Hyperlink
- https://clinicaltrials.gov/ct2/show/NCT02310906
Distributions
- Encoding Format: HTML ; URL: https://clinicaltrials.gov/ct2/show/results/NCT02310906